Most treatments target seizure reduction but do not adequately address the non-seizure-related symptoms of Dravet syndrome, such as cognitive impairment, developmental delays, and behavioral issues .

We are actively recruiting globally for our Phase 3 registration study in Dravet syndrome ... approved treatment for any symptoms in patients with Fragile X syndrome. We are also on track to ...

This potential one-time treatment approach aims to consistently and durably restore UBE3A expression and address the spectrum of symptoms ... ETX101 for Dravet syndrome, which targets the ...

Encoded Therapeutics Inc., a clinical-stage biotechnology company developing genetic medicines for severe central nervous system (CNS) disorders, announced today that it will present new preclinical ...

Harmony Biosciences surpassed $2 billion in cumulative net product revenue less than 5 years on the market, highlighting ...

Phase 3 epilepsy program advancing with X-TOLE2 topline FOS data anticipated in H2 2025– Long-term azetukalner results from X-TOLE open-label ...

Pre-clinical data suggests that targeting Nav1.1 could potentially address the underlying cause and symptoms of Dravet Syndrome. Xenon continues to attract top talent with extensive biopharmaceutical ...

Medications help reduce the number and severity of symptoms. In preclinical and clinical studies, Bexicaserin has shown anti-seizure effects, with a best-in-class profile in Dravet syndrome, ...

The S&P 500 is up more than 19% year to date through the first 10 months of the year. Investors are hoping the Fed has nailed a "soft landing" and the incoming presidential administration, whatever it ...

Dravet syndrome (DS) is a severe form of epilepsy that includes symptoms such as: The first time anyone has a seizure (of any type) the healthcare provider should be notified immediately and ...

Broad-spectrum AEDs often treat generalized seizures, which have symptoms more commonly associated with involuntary ... used to treat seizures associated with Lennox-Gaustat syndrome (LGS) or Dravet ...