Using deep learning techniques, scientists generated an artificial protein that successfully changes its shape to bind and ...

How CD4+ T cells respond to Chikungunya virus may trigger long-lasting joint pain, mimicking autoimmune disease long after infection clears.

Rocket Pharmaceuticals acknowledged the death of a patient in a pivotal trial assessing its Danon disease gene therapy candidate RP-A501, a study that the FDA has placed on clinical hold.

Typically, the goal of ALS treatments is to slow the disease or halt progression. But new data from the antisense oligonucleotide (ASO) jacifusen for FUS-ALS show that two patients went beyond the ...

Mutation of Lis1, a key dynein regulator, can lead to the rare mental developmental disorder lissencephaly, or “smooth brain,” where the brain’s surface lacks the normal folds and grooves, for which ...

Researchers say, “It turns out SSRIs don’t just make our brains happier; they also make our T cells happier—even while ...

Model more closely replicates natural environment of the pancreas, which will be essential for studying diabetes and ...

Treated with an individualized gene-editing therapy that corrects mutations directly on the genome, a patient shows ...

A mass spec-based method for analyzing the structure of lipid nanoparticles could yield new insights that improve vaccine and ...

This week a group of researchers, bioethicists, publishers and theologians are discussing the merits of human heritable ...

Researchers have developed a new suite of genetic tools for cell-type specific targeting to battle brain disease.

Halo Labs believes that by combining with Waters, its ability to expand its platform's reach will enhance drug development ...